Aldeyra Therapeutics reports Phase 3 success with reproxalap for dry eye disease, plans third FDA filing after previous ...

A Singapore-based startup raised a $45 million Series B to start testing a gene therapy in humans next year for a genetic ...

Several members of an FDA advisory committee warned on Monday that new data from studies on long-term use of opioids might ...

PTC Therapeutics announced Monday that its splicing drug for Huntington’s disease met the primary endpoint of a Phase 2 study ...

Vertex said it's gathering momentum with its new product launches, building out new franchises with its sickle cell therapy ...

Function Health is buying Ezra in a bid to create a haven for people who want copious amounts of data on their bodies. The ...

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Deerfield Management is back with its third healthcare venture fund, this time securing more than $600 million to create new ...

J&J's gene therapy bota-vec failed Phase 3 trial for X-linked retinitis pigmentosa vision loss. Follows trend of big pharma ...

Topas Therapeutics reveals first data from celiac disease therapy study, showing promise in immune system retraining with ...

FDA delays Stealth BioTherapeutics PDUFA date amid questions about agency disruption, while other companies like Sanofi and J ...

Initial clinical data from Genocury and EsoBiotec shows promise for in vivo CAR-T therapy, with complete remission in ...